A baby with a rare genetic disorder is thriving after receiving an experimental gene-editing treatment tailored specifically for him. KJ Muldoon, diagnosed with severe CPS1 deficiency, received a CRISPR-based therapy developed by researchers at Children’s Hospital of Philadelphia and Penn Medicine. Using a technique called ‘base editing,’ the treatment corrected the genetic mutation causing his condition. Although long-term effects remain under observation, this breakthrough could pave the way for personalized treatments for other rare genetic disorders. — new from AP News
